Intellia Therapeutics is a genome editing company focused on developing therapeutics utilizing a biological tool known as Clustered, Regularly Interspaced Short Palindromic Repeats (CRISPR)/CRISPR associated 9 (Cas9). This is a technology for genome editing, the process of altering selected sequences of genomic deoxyribonucleic acid. Co. utilizes its CRISPR/Cas9 platform across two areas: in vivo and ex vivo therapies. Co.'s in vivo candidate, NTLA-2001 for the treatment of transthyretin amyloidosis is the delivered CRISPR/Cas9-based therapy to enter clinical evaluation. Co.'s ex vivo applications to address immuno-oncology and autoimmune diseases.
NTLA — Key Stats (updated Friday, July 30, 10:37 AM)